Long-term evaluation parameters in GNE myopathy: a 5-year observational follow-up natural history study
Madoka Mori-Yoshimura, Hiroyuki Yajima, Yasushi Oya, Katsuhiro Mizuno, Satoru Noguchi, Ichizo Nishino, Yuji Takahashi
BMJ Neurology Open Dec 2022, 4 (2) e000362; DOI: 10.1136/bmjno-2022-000362