Persistent neuromuscular junction transmission defects in adults with spinal muscular atrophy treated with nusinersen
W David Arnold, Steven Severyn, Songzhu Zhao, David Kline, Matthew Linsenmayer, Kristina Kelly, Marco Tellez, Amy Bartlett, Sarah Heintzman, Jerry Reynolds, Gary Sterling, Tristan Weaver, Kiran Rajneesh, Arthur H M Burghes, Stephen J Kolb, Bakri Elsheikh
BMJ Neurology Open Aug 2021, 3 (2) e000164; DOI: 10.1136/bmjno-2021-000164